{"id":954,"date":"2023-05-03T17:17:26","date_gmt":"2023-05-03T15:17:26","guid":{"rendered":"https:\/\/www.linkidoc.fr\/blog\/2023\/05\/03\/les-nanoparticules-delivrent-une-therapie-par-arnm-aux-poumons\/"},"modified":"2023-05-03T17:17:28","modified_gmt":"2023-05-03T15:17:28","slug":"les-nanoparticules-delivrent-une-therapie-par-arnm-aux-poumons","status":"publish","type":"post","link":"https:\/\/www.linkidoc.fr\/blog\/2023\/05\/03\/les-nanoparticules-delivrent-une-therapie-par-arnm-aux-poumons\/","title":{"rendered":"Les nanoparticules d\u00e9livrent une th\u00e9rapie par ARNm aux poumons"},"content":{"rendered":"<div>\n<figure class=\"wp-block-image size-full\"><noscript><img loading=\"lazy\" decoding=\"async\" width=\"770\" height=\"534\" src=\"https:\/\/www.linkidoc.fr\/blog\/wp-content\/uploads\/2023\/05\/Les-nanoparticules-delivrent-une-therapie-par-ARNm-aux-poumons.jpg\" alt=\"\" class=\"wp-image-1547977\"  \/><\/noscript><\/figure>\n<p>Des chercheurs du MIT ont d\u00e9velopp\u00e9 des nanoparticules lipidiques tr\u00e8s efficaces pour d\u00e9livrer des th\u00e9rapies d&rsquo;ARNm aux cellules pulmonaires.  L&rsquo;introduction d&rsquo;agents th\u00e9rapeutiques dans les poumons peut \u00eatre difficile, mais il existe une vari\u00e9t\u00e9 de d\u00e9fis m\u00e9dicaux qui pourraient \u00eatre r\u00e9solus en ciblant efficacement les cellules pulmonaires avec des technologies de nanoparticules.  Ces derni\u00e8res particules sont tr\u00e8s efficaces pour d\u00e9livrer de l&rsquo;ARNm qui peut ensuite coder des prot\u00e9ines th\u00e9rapeutiquement utiles dans les poumons.  Jusqu&rsquo;\u00e0 pr\u00e9sent, les chercheurs ont d\u00e9montr\u00e9 que les particules peuvent d\u00e9livrer de l&rsquo;ARNm qui code pour le syst\u00e8me d&rsquo;\u00e9dition de g\u00e8nes CRISPR\/Cas, sugg\u00e9rant que la nouvelle m\u00e9thode pourrait \u00eatre utile dans le traitement de maladies g\u00e9n\u00e9tiques qui affectent les poumons, comme la fibrose kystique.   <\/p>\n<p>Concevoir des nanoparticules capables de traiter les poumons est un d\u00e9fi.  En r\u00e8gle g\u00e9n\u00e9rale, les particules doivent \u00eatre con\u00e7ues de mani\u00e8re \u00e0 pouvoir \u00eatre inhal\u00e9es, puis, une fois qu&rsquo;elles atteignent les cellules cibles, elles doivent \u00eatre capables de livrer avec succ\u00e8s leur cargaison \u00e0 l&rsquo;int\u00e9rieur de la cellule.  Bien qu&rsquo;il puisse \u00eatre difficile d&rsquo;atteindre tous ces param\u00e8tres, le faire avec succ\u00e8s pourrait d\u00e9bloquer de nouveaux traitements pour les maladies pulmonaires, telles que la fibrose kystique.<\/p>\n<p>La technologie de l&rsquo;ARNm a d\u00e9montr\u00e9 son utilit\u00e9 dans les vaccins COVID-19, de sorte que ces chercheurs du MIT ont int\u00e9gr\u00e9 cette technologie dans un nouveau type de nanoparticule qui peut cibler les maladies pulmonaires.  \u00ab\u00a0Il s&rsquo;agit de la premi\u00e8re d\u00e9monstration d&rsquo;une d\u00e9livrance tr\u00e8s efficace d&rsquo;ARN dans les poumons chez la souris\u00a0\u00bb, a d\u00e9clar\u00e9 Daniel Anderson, chercheur impliqu\u00e9 dans l&rsquo;\u00e9tude.  \u00ab\u00a0Nous esp\u00e9rons qu&rsquo;il pourra \u00eatre utilis\u00e9 pour traiter ou r\u00e9parer une gamme de maladies g\u00e9n\u00e9tiques, y compris la fibrose kystique.\u00a0\u00bb<!-- ASYNC UAT M - 300x250(t,r) - --><\/p>\n<p><!-- END ASYNC UAT M - 300x250(t,r) --><\/p>\n<p>Alors que l&rsquo;ARNm lui-m\u00eame pourrait contribuer \u00e0 am\u00e9liorer les probl\u00e8mes caus\u00e9s par des g\u00e8nes d\u00e9fectueux en produisant une prot\u00e9ine qui manquait autrement, par exemple, le syst\u00e8me d&rsquo;\u00e9dition de g\u00e8nes CRISPR\/Cas pourrait supprimer compl\u00e8tement les g\u00e8nes d\u00e9fectueux et les remplacer par une copie fonctionnelle du g\u00e8ne. .  Ces chercheurs ont habilement exploit\u00e9 cela, en incluant dans leurs particules de l&rsquo;ARNm qui code pour les prot\u00e9ines CRISPR\/Cas, permettant aux cellules pulmonaires de cr\u00e9er la machinerie n\u00e9cessaire pour \u00e9diter leur propre mat\u00e9riel g\u00e9n\u00e9tique.<\/p>\n<p>Les lipides qui composent les nanoparticules contiennent un groupe de t\u00eate positif et une queue lipidique n\u00e9gative.  La t\u00eate positive aide \u00e0 lier l&rsquo;ARNm charg\u00e9 n\u00e9gativement et lui permet de s&rsquo;\u00e9chapper de la nanoparticule une fois \u00e0 l&rsquo;int\u00e9rieur de la cellule, tandis que la queue n\u00e9gative permet aux particules de traverser la membrane cellulaire.  Lors de tests sur des souris, les chercheurs ont rapport\u00e9 qu&rsquo;environ 40% des cellules pulmonaires ont \u00e9t\u00e9 trait\u00e9es avec succ\u00e8s avec une dose de particules, qui est pass\u00e9e \u00e0 60% apr\u00e8s trois doses.  Les chercheurs esp\u00e8rent que cette prestation tr\u00e8s efficace fera une diff\u00e9rence positive pour les patients si la th\u00e9rapie parvient \u00e0 la clinique.<\/p>\n<p>\u00c9tudier dans la revue <em>Biotechnologie naturelle<\/em>: Conception combinatoire de nanoparticules pour la d\u00e9livrance d&rsquo;ARNm pulmonaire et l&rsquo;\u00e9dition du g\u00e9nome<\/p>\n<p>Via : MIT<\/p>\n<p>Image : iStock, \u00e9dit\u00e9 par MIT News<\/p>\n<p><!--TrendMD v2.4.8--><\/div>\n","protected":false},"excerpt":{"rendered":"<p>Des chercheurs du MIT ont d\u00e9velopp\u00e9 des nanoparticules lipidiques tr\u00e8s efficaces pour d\u00e9livrer des th\u00e9rapies d&rsquo;ARNm aux cellules pulmonaires. L&rsquo;introduction<\/p>\n","protected":false},"author":1,"featured_media":955,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[1287,54,1286,12,1285,802,1288,1239,86],"class_list":["post-954","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-non-classe","tag-arnm","tag-aux","tag-delivrent","tag-les","tag-nanoparticules","tag-par","tag-poumons","tag-therapie","tag-une","generate-columns","tablet-grid-50","mobile-grid-100","grid-parent","grid-50"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.2 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Les nanoparticules d\u00e9livrent une th\u00e9rapie par ARNm aux poumons - Blog Linkidoc : consultant e-sant\u00e9<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.linkidoc.fr\/blog\/2023\/05\/03\/les-nanoparticules-delivrent-une-therapie-par-arnm-aux-poumons\/\" \/>\n<meta property=\"og:locale\" content=\"fr_FR\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Les nanoparticules d\u00e9livrent une th\u00e9rapie par ARNm aux poumons - Blog Linkidoc : consultant e-sant\u00e9\" \/>\n<meta property=\"og:description\" content=\"Des chercheurs du MIT ont d\u00e9velopp\u00e9 des nanoparticules lipidiques tr\u00e8s efficaces pour d\u00e9livrer des th\u00e9rapies d&rsquo;ARNm aux cellules pulmonaires. 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